Amber

RNA writing (trans-splicing) for correction of genetic diseases

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What they do

Problem

Genetic diseases caused by faulty genes require effective ways to correct or bypass harmful mutations.

Solution

The company uses RNA writing via trans-splicing to repair or replace defective RNA transcripts to correct genetic disease at the RNA level.

Who it's for

Biopharma companies and clinical researchers developing RNA-based therapies for patients with genetic diseases.